
PALO ALTO INVESTORS LP
Latest 13F filing data - Q3 2025
Holdings (Top positions)
| Stock | Ticker | ||
|---|---|---|---|
![]() | AGIO | 265K | $10.66M |
![]() | ALDX | 225K | $1.18M |
![]() | IRON | 224K | $14.82M |
![]() | BCYC | 221K | $1.71M |
![]() | PRQR | 189K | $402.16K |
![]() | BIIB | 186K | $26.01M |
![]() | ALKS | 184K | $5.52M |
![]() | AKTX | 146K | $147.48K |
![]() | TVTX | 111K | $2.65M |
![]() | RNA | 110K | $4.79M |
![]() | STOK | 105K | $2.48M |
![]() | MIRM | 65K | $4.74M |
![]() | ORKA | 60K | $791.31K |
![]() | UTHR | 58K | $24.39M |
![]() | ALGN | 46K | $5.73M |
![]() | CRSP | 41K | $2.67M |
![]() | EW | 34K | $2.62M |
![]() | ALNY | 32K | $14.74M |
![]() | URGN | 25K | $488.77K |
![]() | BNTX | 20K | $1.93M |

Agios Pharmaceuticals, Inc.
AGIO
Shares Held
265K
Value
$10.66M

Aldeyra Therapeutics, Inc.
ALDX
Shares Held
225K
Value
$1.18M

Disc Medicine, Inc.
IRON
Shares Held
224K
Value
$14.82M

Bicycle Therapeutics plc
BCYC
Shares Held
221K
Value
$1.71M

ProQR Therapeutics N.V.
PRQR
Shares Held
189K
Value
$402.16K

Biogen Inc.
BIIB
Shares Held
186K
Value
$26.01M

Alkermes plc
ALKS
Shares Held
184K
Value
$5.52M

Akari Therapeutics, Plc
AKTX
Shares Held
146K
Value
$147.48K

Travere Therapeutics, Inc.
TVTX
Shares Held
111K
Value
$2.65M

Avidity Biosciences, Inc.
RNA
Shares Held
110K
Value
$4.79M

Stoke Therapeutics, Inc.
STOK
Shares Held
105K
Value
$2.48M

Mirum Pharmaceuticals, Inc.
MIRM
Shares Held
65K
Value
$4.74M

Oruka Therapeutics, Inc.
ORKA
Shares Held
60K
Value
$791.31K

United Therapeutics Corporation
UTHR
Shares Held
58K
Value
$24.39M

Align Technology, Inc.
ALGN
Shares Held
46K
Value
$5.73M

CRISPR Therapeutics AG
CRSP
Shares Held
41K
Value
$2.67M

Edwards Lifesciences Corporation
EW
Shares Held
34K
Value
$2.62M

Alnylam Pharmaceuticals, Inc.
ALNY
Shares Held
32K
Value
$14.74M

UroGen Pharma Ltd.
URGN
Shares Held
25K
Value
$488.77K

BioNTech SE
BNTX
Shares Held
20K
Value
$1.93M
